Prion Disease Treatment: Milestone Research and Hope

April 7, 2025

The quest for effective prion disease treatment has gained significant momentum, illuminating a path toward hope for patients afflicted by these rare yet devastating disorders.Recent groundbreaking research led by a team at the Broad Institute of MIT and Harvard suggests that gene editing for prion disease may be on the horizon, aiming to mitigate the effects of harmful misfolded proteins in the brain.
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